Emixustat hydrochloride is a non-retinoid small molecule inhibitor of RPE65 (retinal pigment epithelium-specific 65 kDa protein, also known as retinoid isomerohydrolase), and reduces visual chromophore biosynthesis responsible for the accumulation of toxic retinal byproducts.
Emixustat hydrochloride is a non-retinoid small molecule inhibitor of RPE65 (retinal pigment). Epithelium-specific 65 kDa protein, also known retinal pigment as retinoid isomerohydrolase. Emixustat hydrochloride reduces visual chromophore biosynthesis responsible for the accumulation of toxic retinal byproducts.