children s health issues
Niemann Pick Disease
Treatment of Niemann Pick Disease
Possible bone marrow transplantation, stem cell transplantation, and enzyme replacement None of the types of Niemann-Pick disease can be cured, and children tend to die of infection or progressive dysfunction of the central nervous system (the brain and spinal cord). Currently, some therapies that may slow or halt the progression of symptoms, such as bone marrow transplantation, Stem Cell Transplantation , and enzyme replacement, are being studied. 