This is compelling evidence of CRISPR's adaptability and potential as a versatile therapeutic platform technology, offering the prospect of addressing a diverse range of diseases with a single, refined delivery method.
For instance, Intellia's remarkable transition from one liver-targeted therapy to another was achieved by simply modifying the guide RNA to direct the DNA edit's location. This is compelling evidence of CRISPR's adaptability and potential as a versatile therapeutic platform technology, offering the prospect of addressing a diverse range of diseases with a single, refined delivery method.